The French compassionate programme of elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis with advanced lung disease and no F508del CFTR variant
Pierre-Régis Burgel, Isabelle Sermet-Gaudelus, Isabelle Durieu, Reem Kanaan, Julie Macey, Dominique Grenet, Michele Porzio, Nathalie Coolen-Allou, Raphael Chiron, Christophe Marguet, Benoit Douvry, Nadine Dufeu, Isabelle Danner-Boucher, Pierre Foucaud, Lydie Lemonnier, Emmanuelle Girodon, Jennifer Da Silva, Clémence Martin, on behalf of the French CF Reference Network study group,
, Claire Andrejak, Pascaline Priou, Bénédicte Richaud-Thiriez, Julie Macey, Sylvie Montcouquiol, Benoit Douvry, Natacha Remus, Annlyse Fanton, Nathalie Coolen-Allou, Elsa Gachelin, Constance Vuillard, Camille Audousset, Louise Duthoit, Elisabeth Bellet-Fraysse, Jeanne Languepin, Isabelle Durieu, Raphaele Nove-Josserand, Camille Ohlmann, Quitterie Raynaud, Nadine Dufeu, Raphael Chiron, Yves Billon, Isabelle Danner-Boucher, Adrien Tissot, Sylvie Leroy, Frédérique Aubourg, Espérie Burnet, Pierre-Régis Burgel, Nicolas Carlier, Jennifer Da Silva, Isabelle Fajac, Emmanuelle Girodon, Reem Kanaan, Isabelle Honoré, Clémence Martin, Muriel Le Bourgeois, Isabelle Sermet-Gaudelus, Laurence Le Clainche-Viala, Harriet Corvol, Clémence Dehillotte, Pierre Foucaud, Lydie Lemonnier, Graziella Brinchault, Bruno Ravoninjatovo, Jean Le Bihan, Sophie Ramel, Christophe Marguet, Michele Porzio, Laurence Weiss, Dominique Grenet, Sandra de Miranda, Laure Cosson, Julie Mankikian, Delphine Pouradier
European Respiratory Journal May 2023, 61 (5) 2202437; DOI: 10.1183/13993003.02437-2022